Englander Institute for Precision Medicine

Human pancreatic progenitor organoids define genetic and epigenetic barriers to early PDAC transformation.

TitleHuman pancreatic progenitor organoids define genetic and epigenetic barriers to early PDAC transformation.
Publication TypeJournal Article
Year of Publication2026
AuthorsZhang X, Wong W, Cho HS, Yang D, Dixon G, Luo R, Liu D, Torre D, Umeda S, González F, Askan G, Yavas A, Damodaran JRavichandr, Rickert RW, Kappagantula R, Pan FCheng, Aveson VG, Grimont A, Fall WB, Wang X, Pulecio J, Kaplan SJ, Pan H, Peng XLaura, Yeh JJen, Leach SD, Iacobuzio-Donahue CA, Chandwani R, Leslie CS, Huangfu D
JournalDev Cell
Date Published2026 May 19
ISSN1878-1551
Abstract

The lack of accurate human models that recapitulate pancreatic ductal adenocarcinoma (PDAC) initiation has hindered therapeutic development. Using pluripotent stem cell-derived pancreatic progenitor organoids, we established a human PDAC model that faithfully reproduces the genetic, epigenetic, and transcriptomic trajectories of tumor initiation and progression, validated against clinical datasets and tumor histopathology. We demonstrate that CDKN2A loss, which is nearly universal in patients but dispensable in mouse models, is essential for neoplastic transformation when combined with KRAS and TP53 mutations, whereas SMAD4 loss promotes tumor progression. Multi-omics profiling reveals epigenetic repression of the pancreatic lineage program during PDAC initiation, alongside AP-1-driven chromatin remodeling. We identify TET1 suppression as a mechanistic link between oncogenic ERK signaling and hypermethylation of essential pancreatic transcription factors. This model captures genetic and epigenetic determinants of human PDAC, reveals antagonism between oncogenic and lineage restriction programs, and supports TET-based lineage restoration as a potential early intervention strategy.

DOI10.1016/j.devcel.2026.04.012
Alternate JournalDev Cell
PubMed ID42161274
PubMed Central IDPMC13196429
Grant ListP30 CA008748 / CA / NCI NIH HHS / United States
R01 DK096239 / DK / NIDDK NIH HHS / United States
R01 HD111256 / HD / NICHD NIH HHS / United States

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